rare diseases

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Biotech

Glycomine's $115M series C to fund genetic disorder ph. 2 plans

Glycomine has bagged a $115 million series C to continue the progress of its lead candidate through phase 2 development for a rare genetic disorder.
James Waldron Apr 16, 2025 9:20am
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Spruce inks deal for BioMarin asset, plans 2026 approval filing

Apr 15, 2025 10:29am
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AstraZeneca's $800M rare disease bet hits primary phase 3 goal

Mar 17, 2025 7:25am
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Clario acquires WCG's neuro-focused eCOA business

Mar 12, 2025 3:40pm
cows

Gene therapy spares mice and calf from maple syrup urine disease

Mar 4, 2025 5:15am
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Regeneron gene therapy restores hearing in 10 of 11 children

Feb 24, 2025 3:00pm