rare diseases

Model skeleton in an anatomy classroom
Research

Antibody strengthens bones in mice with brittle bone disease

The antibody targets Siglec-15, a protein found on the surface of bone-destroying cells called osteoclasts.
Darren Incorvaia Jul 30, 2025 2:54pm
FDA stop sign
Favicon Fierce Pharma

FDA snubs Ultragenyx gene therapy over manufacturing issues

Jul 14, 2025 10:16am
relay

Rallybio shifts gears, cashing out of Recursion pact

Jul 8, 2025 8:59am
Graphic image of an arrow nailing the bullseye of a target

Cogent hits primary endpoint, building case for Blueprint rival

Jul 7, 2025 9:16am
Congress senate house government US
Favicon Fierce Pharma

Senate revives Orphan Cures Act in Trump's tax bill

Jun 30, 2025 10:09am
ice skate on the ice

Minovia skates SPAC-wards into public market

Jun 25, 2025 10:33am