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Huntington disease
Biotech
2024's top 10 clinical trial flops
Fierce Biotech recounts the top 10 clinical trial failures of 2024 that sent ripples across the industry.
James Waldron
Feb 18, 2025 3:00am
Novartis pays PTC $1B upfront for midphase Huntington's program
Dec 2, 2024 7:53am
uniQure's interim data shows gene therapy slows Huntington’s
Jul 9, 2024 9:25am
Sage's dalzanemdor trial design leaves efficacy question unclear
Jun 11, 2024 8:28am
VectorY raises $138M to push forward ALS program
Nov 13, 2023 10:26am
JPM23: Annexon looks for '2 ways to win' in Huntington's trial
Jan 11, 2023 12:55pm