gene therapy

Fierce Pharma

2nd patient dies after Sarepta's DMD gene therapy Elevidys

Sarepta has suspended giving Elevidys to non-ambulatory DMD patients in the commercial setting while it seeks FDA approval of a risk mitigation plan.

Angus Liu Jun 16, 2025 10:58am

An artists depiction of DNA molecules made up of tiny particles

RegenXBio links DMD gene therapy to improved outcomes

Jun 5, 2025 8:52am

Make a delay and accumulation of outstanding tasks Full stop

Rocket crashes as gene therapy patient dies, FDA imposes hold

May 27, 2025 9:49am

a lot of scissors

Gene editor shelves sole clinical asset, lays off 25% of staff

May 19, 2025 2:28pm

Close-up of human eye

Atsena gene therapy hits safety goals, closes retinal splits

May 19, 2025 12:59pm

gene therapy AAV adeno-associated viruses

Neurogene details death in Rett syndrome gene therapy trial

May 16, 2025 3:00pm