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Friedreich's Ataxia
Biotech
Lexeo locks in pivotal trial plan as gene therapy data accrue
Lexeo linked the gene therapy to improvements on outcomes it plans to use as co-primary endpoints in a registrational trial.
Nick Paul Taylor
Apr 7, 2025 9:37am
PTC bounces back with positive data on FA prospect vatiquinone
Oct 8, 2024 9:34am
Lexeo links gene therapy to improvements in rare heart disease
Jul 15, 2024 9:46am
FDA picks Denali, Neurogene and more for rare disease program
Jun 4, 2024 2:51pm
Larimar's Friedreich's ataxia program free at last from FDA hold
May 21, 2024 9:55am
After pair of failures, PTC finds path for Friedreich ataxia med
Mar 1, 2024 9:20am
