Duchenne muscular dystrophy (DMD)

sarepta building

Fierce Pharma

FDA backtracks on Sarepta's gene therapy Elevidys in DMD

The agency said that it had concluded that the death of an 8-year-old was not related to Elevidys but addressed none of the three prior deaths.

Angus Liu Jul 28, 2025 6:02pm

Fierce Pharma

FDA contemplates pulling Sarepta’s Elevidys from market

Jul 18, 2025 3:10pm

Businessman about to be crushed by falling dominos

Sarepta overhaul includes 500 layoffs, gene therapy program cuts

Jul 16, 2025 4:59pm

Graphic image of a red thumbs down against a blue background

FDA rejects Capricor’s DMD cell therapy, asks for more data

Jul 11, 2025 9:18am

Goal disorientation and lack of vision

UPDATED: Taiho’s discontinues ph. 3 trial after DMD miss

Jul 8, 2025 10:17am

FDA

Fierce Pharma

FDA investigates 2 deaths after Sarepta Duchenne gene therapy

Jun 25, 2025 10:26am