base editing

Network of blood vessels against a white background

Research

Custom gene editor fixes mutation causing deadly disease in mice

Swapping out a mutant letter in the ACTA2 gene saved the lives of mice with an ultrarare vascular disease, while all untreated mice died.

Darren Incorvaia Sep 11, 2025 1:48pm

NIH

NIH gene editing fixes Tay-Sachs mutation in mice

Aug 19, 2025 4:22pm

roadmap hurdles

Verve posts clean PCSK9 editor profile, teeing up Lilly decision

Apr 14, 2025 7:00am

DNA strand gene editing

Beam hits hemoglobin goal in first base editing clinical data

Nov 5, 2024 9:00am

Graphic of someone in a boat navigating the rise and fall of different data riding data plots like a wave

Verve halts VERVE-101 enrollment, focuses on 2nd PCSK9 editor

Apr 2, 2024 7:00am

An artists concept of gene editing A DNA strand appears in blue with edited regions in red

PKU in mice treated with base and prime editing

Nov 3, 2023 1:08pm